Paediatric non-neuronopathic Gaucher disease: recommendations for treatment and monitoring

  • A Baldellou
  • , G Andria
  • , PE Campbell
  • , J Charrow
  • , IJ Cohen
  • , GA Grabowski
  • , CM Harris
  • , P Kaplan
  • , K McHugh
  • , E Mengel
  • , A Vellodi

Research output: Contribution to journalArticlepeer-review

Original languageEnglish
Pages (from-to)67-75
Number of pages0
JournalEuropean Journal of Pediatrics
Volume163
Issue number2
DOIs
Publication statusPublished - 2004

Keywords

  • Gaucher disease
  • management
  • monitoring
  • paediatric
  • quality-of-life

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